Research in the Grousbeck Gene Therapy Center and Vandenberghe Lab is focused on developing and translating genetic therapies to the clinic with an emphasis on blindness and other neurosensory disorders. We aim at defining, characterizing and overcoming hurdles on the path of gene therapies to clinical applications through:
- The study of the biology of, and host response to genetic therapy.
- The development of enabling gene transfer technologies.
- The translation of specific therapeutic programs.
Please visit Gene Transfer Vector Core (GTVC) section. GTVC offers research grade vector preparation and related services for in vitro and in vivo applications.
To learn more about the Vandenberghe Lab, please visit: http://www.vdb-lab.org/